OUR REACH
The Pediatric foundation for rare diseases has a global presence, with children from around the globe benefiting from our initiative.
ABOUT OUR FOUNDATION
The Pediatric foundation for rare diseases was born after our son was diagnosed with Metachromatic Leukodystrophy. We were told there were no options and no hope.
We quickly learned that clinical trials have very strict guidelines and not all patients will qualify based on their symptoms. We are on a mission to fund treatment opportunities for kids who do not fit the mold of a clinical trial.
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Our current project is looking to break that mold and fund a clinical trial for gene therapy for symptomatic kids with Metachromatic Leukodystrophy. We believe that no child shall be told there are no options.
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Our mission is to fund research and innovative therapies for pediatric patients battling rare diseases who have otherwise been told there is no hope. We offer hope.
